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Naslov Safety and Efficacy of Pegcetacoplan in Adult Patients with Paroxysmal Nocturnal Hemoglobinuria over 48 Weeks: 307 Open-Label Extension Study (Article)
Autori Patriquin Christopher J  Bogdanovic Andrija D  Griffin Morag  Kelly Richard J  Maciejewski Jaroslaw P  Mulherin Brian  De Latour Regis Peffault  Roeth Alexander  Selvaratnam Veena  Szer Jeffrey  Al Adhami Mohammed  Horneff Regina  Tan Lisa  Yeh Michael  Panse Jens 
Info ADVANCES IN THERAPY, (2024), vol. 41 br. 5, str. 2050-2069
Projekat Apellis Pharmaceuticals
Ispravka ISI/Web of Science   Članak   Elečas   Rang časopisa   Citati:
Naslov Long-Term Safety and Efficacy of Pegcetacoplan Treatment in Adults with Paroxysmal Nocturnal Hemoglobinuria (Meeting Abstract)
Autori Patriquin Christopher J  Bogdanovic Andrija D  Griffin Morag  Kelly Richard  Maciejewski Jaroslaw P  Mulherin Brian  De Latour Regis Peffault  Roeth Alexander  Selvaratnam Veena  Szer Jeffrey  Savage Jessica  Horneff Regina  Tan Lisa  Yeh Michael  Panse Jens 
Info ONCOLOGY RESEARCH AND TREATMENT, (2023), vol. 46 br. , Suppl. 5, str. 203-204
Ispravka ISI/Web of Science   Elečas   Rang časopisa  
Naslov Long-Term Safety and Efficacy of Pegcetacoplan Treatment in Adults with Paroxysmal Nocturnal Hemoglobinuria (Meeting Abstract)
Autori Patriquin Christopher J  Bogdanovic Andrija D  Griffin Morag  Kelly Richard  Maciejewski Jaroslaw P  Mulherin Brian  De Latour Regis Peffault  Roeth Alexander  Selvaratnam Veena  Szer Jeffrey  Savage Jessica  Horneff Regina  Tan Lisa  Yeh Michael  Panse Jens 
Info BLOOD, (2022), vol. 140 br. , Suppl. 1, str. 2921-2923
Ispravka ISI/Web of Science   Članak   Elečas   Rang časopisa  
Naslov Enzyme replacement therapy with taliglucerase alfa: 36-month safety and efficacy results in adult patients with Gaucher disease previously treated with imiglucerase (Article)
Autori Pastores Gregory M  Shankar Suma P  Petakov Milan S  Giraldo Pilar  Rosenbaum Hanna  Amato Dominick J  Szer Jeffrey  Chertkoff Raul  Brill-Almon Einat  Zimran Ari 
Info AMERICAN JOURNAL OF HEMATOLOGY, (2016), vol. 91 br. 7, str. 661-665
Projekat Protalix BioTherapeutics; Pfizer
Ispravka ISI/Web of Science   Članak   Elečas   Rang časopisa   Citati: ISI/Web of Science   Scopus  
Naslov A Phase 3, multicenter, open-label, switchover trial to assess the safety and efficacy of taliglucerase alfa, a plant cell-expressed recombinant human glucocerebrosidase, in adult and pediatric patients with Gaucher disease previously treated with imiglucerase (Article)
Autori Pastores Gregory M  Petakov Milan S  Giraldo Pilar  Rosenbaum Hanna  Szer Jeffrey  Deegan Patrick B  Amato Dominick J  Mengel Eugen  Tan Ee Shien  Chertkoff Raul  Brill-Almon Einat  Zimran Ari 
Info BLOOD CELLS MOLECULES AND DISEASES, (2014), vol. 53 br. 4, str. 253-260
Projekat Protalix BioTherapeutics; Pfizer
Ispravka ISI/Web of Science   Članak   Elečas   Rang časopisa   Citati: ISI/Web of Science   Scopus  
Naslov Plant cell-expressed recombinant glucocerebrosidase: Taliglucerase alfa as therapy for Gaucher disease in adults patients previously treated with imiglucerase: 24-month results (Meeting Abstract)
Autori Pastores Gregory M  Shankar Suma P  Szer Jeffrey  Petakov Milan S  Cox Timothy M  Giraldo Pilar  Rosenbaum Hanna  Amato Dominick J  Mengel Eugen  Chertkoff Raul  Almon-Brill Einat  Zimran Ari 
Info MOLECULAR GENETICS AND METABOLISM, (2013), vol. 108 br. 2, str. S73-S74
Ispravka ISI/Web of Science   Članak   Elečas   Rang časopisa   Citati: ISI/Web of Science  
Naslov PLANT CELL EXPRESSED RECOMBINANT GLUCOCEREBROSIDASE - TALIGLUCERASE ALFA AS THERAPY FOR GAUCHER DISEASE IN PATIENTS PREVIOUSLY TREATED WITH IMIGLUCERASE (Meeting Abstract)
Autori Pastores Gregory M  Szer Jeffrey  Petakov Milan S  Cox Timothy M  Giraldo Pilar  Rosenbaum Hanna  Amato Dominick J  Mengel Eugen  Chertkoff Raul  Almon-Brill Einat  Zimran Ari 
Info JOURNAL OF INHERITED METABOLIC DISEASE, (2012), vol. 35 br. , Suppl. 1, str. S100-S100
Ispravka ISI/Web of Science   Elečas   Rang časopisa   Citati: ISI/Web of Science  
Naslov Plant Cell Expressed Recombinant Glucocerebrosidase - Taliglucerase alfa as Therapy for Gaucher Disease in Patients Previously Treated with Imiglucerase (Meeting Abstract)
Autori Pastores Gregory M  Fernhoff Paul M  Szer Jeffrey  Petakov Milan S  Cox Timothy M  Giraldo Pilar  Rosenbaum Hanna  Amato Dominick J  Mengel Eugen  Chertkoff Raul  Almon-Brill Einat  Zimran Ari 
Info MOLECULAR GENETICS AND METABOLISM, (2012), vol. 105 br. 2, str. S50-S50
Ispravka ISI/Web of Science   Članak   Elečas   Rang časopisa   Citati: ISI/Web of Science  
Naslov Plant Cell Expressed Recombinant Glucocerebrosidase - taliglucerase alfa - as Therapy for Gaucher Disease in Patients Previously Treated with imiglucerase (Meeting Abstract)
Autori Pastores Gregory M  Fernhoff Paul M  Szer Jeffrey  Petakov Milan S  Cox Timothy M  Giraldo Pilar  Rosenbaum Hanna  Amato Dominick J  Mengel Eugen  Chertkoff Raul  Almon-Brill Einat  Zimran Ari 
Info MOLECULAR GENETICS AND METABOLISM, (2011), vol. 102 br. 2, str. S33-S33
Ispravka ISI/Web of Science   Članak   Elečas   Rang časopisa   Citati: ISI/Web of Science  
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