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Autori: Giraldo Pilar

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Naslov Pivotal trial with plant cell-expressed recombinant glucocerebrosidase, taliglucerase alfa, a novel enzyme replacement therapy for Gaucher disease (Erratum - errors in Affiliations - vol 118, pg 5767, 2011) (Correction)
Autori Zimran Ari  Brill-Almon Einat  Chertkoff Raul  Petakov Milan S  Blanco-Favela Francisco  Munoz Eduardo Terreros  Solorio Meza Sergio Eduardo  Amato Dominick J  Duran Gloria  Giona Florina  Heitner Rene  Rosenbaum Hanna  Giraldo Pilar  Mehta Atul  Park Glen  Phillips Mici  Elstein Deborah  Altarescu Gheona  Szleifer Mali  Hashmueli Sharon  Aviezer David 
Info BLOOD, (2012), vol. 119 br. 19, str. 4577-4577
Ispravka ISI/Web of Science   Elečas   Rang časopisa   Citati: ISI/Web of Science  
Naslov Plant Cell Expressed Recombinant Glucocerebrosidase - Taliglucerase alfa as Therapy for Gaucher Disease in Patients Previously Treated with Imiglucerase (Meeting Abstract)
Autori Pastores Gregory M  Fernhoff Paul M  Szer Jeffrey  Petakov Milan S  Cox Timothy M  Giraldo Pilar  Rosenbaum Hanna  Amato Dominick J  Mengel Eugen  Chertkoff Raul  Almon-Brill Einat  Zimran Ari 
Info MOLECULAR GENETICS AND METABOLISM, (2012), vol. 105 br. 2, str. S50-S50
Ispravka ISI/Web of Science   Članak   Elečas   Rang časopisa   Citati: ISI/Web of Science  
Naslov Plant Cell Expressed Recombinant Glucocerebrosidase - taliglucerase alfa - as Therapy for Gaucher Disease in Patients Previously Treated with imiglucerase (Meeting Abstract)
Autori Pastores Gregory M  Fernhoff Paul M  Szer Jeffrey  Petakov Milan S  Cox Timothy M  Giraldo Pilar  Rosenbaum Hanna  Amato Dominick J  Mengel Eugen  Chertkoff Raul  Almon-Brill Einat  Zimran Ari 
Info MOLECULAR GENETICS AND METABOLISM, (2011), vol. 102 br. 2, str. S33-S33
Ispravka ISI/Web of Science   Članak   Elečas   Rang časopisa   Citati: ISI/Web of Science  
Naslov Peripheral neuropathy in adult type 1 Gaucher disease: a 2-year prospective observational study (Article)
Autori Biegstraaten Marieke  Mengel Eugen  Marodi Laszlo  Petakov Milan S  Niederau Claus  Giraldo Pilar  Hughes Derralyn  Mrsic Mirando  Mehta Atul  Hollak Carla EM  van Schaik Ivo N 
Info BRAIN, (2010), vol. 133 br. , str. 2909-2919
Projekat European Working Group on Gaucher Disease (EWGGD) ; Actelion Pharmaceuticals Ltd ; Actelion Pharmaceuticals Ltd, Allschwil, Switzerland
Ispravka ISI/Web of Science   Članak   Elečas   Rang časopisa   Citati: ISI/Web of Science   Scopus  
Naslov Polyneuropathy in Type 1 Gaucher disease: A two-year, multinational, prospective observational study (Meeting Abstract)
Autori Biegstraaten Marieke  Mengel Eugen  Marodi Laszlo  Petakov Milan S  Niederau Claus  Giraldo Pilar  Hughes Derralyn  Mrsic Mirando  Mehta Atul  Hollak Carla EM  van Schaik Ivo N 
Info MOLECULAR GENETICS AND METABOLISM, (2010), vol. 99 br. 2, str. 14-
Ispravka ISI/Web of Science   Članak   Elečas   Rang časopisa   Citati: ISI/Web of Science  
Naslov Prevalence of polyneuropathy in adult type 1 Gaucher disease (GD1): A multinational prospective observational study (Meeting Abstract)
Autori Hollak Carla EM  Biegstraaten Marieke  van Schaik Ivo N  Mengel Eugen  Marodi Laszlo  Petakov Milan S  Niederau Claus  Giraldo Pilar  Hughes Derralyn  Mrsic Mirando  Mehta Atul 
Info JOURNAL OF INHERITED METABOLIC DISEASE, (2007), vol. 30 br. , Suppl. Suppl. 1 , str. 107 -107
Ispravka ISI/Web of Science   Članak   Elečas   Rang časopisa   Citati: ISI/Web of Science   Scopus  
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