Autori: Baranello Giovanni
Naslov | Clinical Trial Readiness for Spinal Muscular Atrophy: Experience of an International Educational-Training Initiative (Article) |
Autori | Tizzano Eduardo F Christie-Brown Vanessa Baranello Giovanni Germanenko Olga Gray Allyson Krstic Marija Lilien Charlotte Patel Hinal Servais Laurent Scoto Mariacristina |
Info | JOURNAL OF NEUROMUSCULAR DISEASES, (2022), vol. 9 br. 6, str. 809-820 |
Projekat | Cure SMA Industry Consortium (IC) in the US; AveXis, Inc; Biogen; Genentech/Roche Pharmaceuticals; Novartis; Astellas Pharmaceuticals; Cytokinetics Inc; Ionis Pharmaceuticals, Inc.; Scholar Rock |
Ispravka | ISI/Web of Science Članak Elečas Rang časopisa Citati: ISI/Web of Science |
Naslov | Amifampridine safety and efficacy in spinal muscular atrophy ambulatory patients: a randomized, placebo-controlled, crossover phase 2 trial (Article; Early Access) |
Autori | Bonanno Silvia Giossi Riccardo Zanin Riccardo Porcelli Valentina Iannacone Claudio Baranello Giovanni Ingenito Gary Iyadurai Stanley Stevic Zorica D Peric Stojan Z Maggi Lorenzo |
Info | JOURNAL OF NEUROLOGY, (2022), vol. br. , str. - |
Projekat | Catalyst Pharmaceuticals, Inc. |
Ispravka | ISI/Web of Science Članak Elečas Rang časopisa Citati: ISI/Web of Science Scopus |