@ARTICLE{
author={Patriquin Christopher J,Bogdanovic Andrija D,Griffin Morag,Kelly Richard J,Maciejewski Jaroslaw P,Mulherin Brian,De Latour Regis Peffault,Roeth Alexander,Selvaratnam Veena,Szer Jeffrey,Al Adhami Mohammed,Horneff Regina,Tan Lisa,Yeh Michael,Panse Jens},
year={2024},
title={Safety and Efficacy of Pegcetacoplan in Adult Patients with Paroxysmal Nocturnal Hemoglobinuria over 48 Weeks: 307 Open-Label Extension Study},
journal={ADVANCES IN THERAPY},
volume={41},
number={5},
pages={2050-2069},
document_type={Article},
} 

@ARTICLE{
author={Pastores Gregory M,Shankar Suma P,Petakov Milan S,Giraldo Pilar,Rosenbaum Hanna,Amato Dominick J,Szer Jeffrey,Chertkoff Raul,Brill-Almon Einat,Zimran Ari},
year={2016},
title={Enzyme replacement therapy with taliglucerase alfa: 36-month safety and efficacy results in adult patients with Gaucher disease previously treated with imiglucerase},
journal={AMERICAN JOURNAL OF HEMATOLOGY},
volume={91},
number={7},
pages={661-665},
document_type={Article},
} 

@ARTICLE{
author={Pastores Gregory M,Petakov Milan S,Giraldo Pilar,Rosenbaum Hanna,Szer Jeffrey,Deegan Patrick B,Amato Dominick J,Mengel Eugen,Tan Ee Shien,Chertkoff Raul,Brill-Almon Einat,Zimran Ari},
year={2014},
title={A Phase 3, multicenter, open-label, switchover trial to assess the safety and efficacy of taliglucerase alfa, a plant cell-expressed recombinant human glucocerebrosidase, in adult and pediatric patients with Gaucher disease previously treated with imiglucerase},
journal={BLOOD CELLS MOLECULES AND DISEASES},
volume={53},
number={4},
pages={253-260},
document_type={Article},
}