@ARTICLE{
author={Dong Thomas,Hao Siyuan,Milacic Iva,Gray Steven,Chen Xin},
year={2026},
title={Encouraging Results Support Ongoing Development of AAV-Mediated Gene Therapy for Adenylosuccinate Lyase Deficiency},
journal={MOLECULAR THERAPY},
volume={34},
number={5},
pages={3466-3467},
document_type={Meeting Abstract},
} 

