@ARTICLE{
author={Tizzano Eduardo F,Christie-Brown Vanessa,Baranello Giovanni,Germanenko Olga,Gray Allyson,Krstic Marija,Lilien Charlotte,Patel Hinal,Servais Laurent,Scoto Mariacristina},
year={2022},
title={Clinical Trial Readiness for Spinal Muscular Atrophy: Experience of an International Educational-Training Initiative},
journal={JOURNAL OF NEUROMUSCULAR DISEASES},
volume={9},
number={6},
pages={809-820},
document_type={Article},
} 

